Abstract
BACKGROUND: EU legislation is encouraging pharmaceutical companies to develop drugs for rare conditions, but their often high cost, and potential for long-term administration has led to debate about their affordability and cost-effectiveness. AIM: To investigate how many drugs are in development for very rare conditions. METHODS: We defined very rare conditions as having a prevalence of
Original language | English |
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Pages (from-to) | 291-295 |
Number of pages | 5 |
Journal | QJM |
Volume | 100 |
Early online date | 27 Mar 2007 |
DOIs | |
Publication status | Published - 27 Mar 2007 |