AAV-mediated liver-directed gene therapy for Acute Intermittent Porphyria: It is safe but is it effective?

Nicola Brunetti-Pierri, Philip N Newsome

Research output: Contribution to journalEditorialpeer-review

4 Citations (Scopus)
Original languageEnglish
JournalJournal of Hepatology
Volume65
Issue number4
Early online date12 Jul 2016
DOIs
Publication statusPublished - Oct 2016

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